Table 1

Classification of osteopetrotic conditions, modified from the Nosology and Classification of Genetic Skeletal disorders (2006 revision)[2]

Condition
Inheritance
OMIM No
Gene
Mutation mechanism
Protein
Rodent model

Osteopetrosis, severe neonatal or infantile forms
AR
259700
TCIRG1
Loss of function
Subunit of V-ATPase pump
Oc/oc
Tcirg1-/-





AR

CLCN7
Loss of function
Chloride channel
Clcn7-/-





AR

OSTM1
Loss of function
Osteopetrosis associated transmembrane protein
Gl/gl





AR

RANKL
Loss of function
Receptor Activator for Nuclear Factor κ B Ligand
Tnfsfl 1-/-





AR

RANK
Loss of function
Receptor Activator for Nuclear Factor κ B
Tnfrsf11a-/-

Osteopetrosis, intermediate form
AR
259710
CLCN7

Chloride channel






AR

PLEKHM1
Loss of function
Pleckstrin homology domain containing family M, member 1
ia rat

Osteopetrosis with renal tubular acidosis
AR
259730
CAII
Loss of function
Carbonic anhydrase II


Osteopetrosis, late-onset form ('Albers-Schönberg disease')
AD
166600
CLCN7
Dominant negative
Chloride channel


Osteopetrosis with ectodermal dysplasia and immune defect (OLEDAID)
XL
300301
IKBKG (NEMO)
Loss of function
Inhibitor of kappa light polypeptide gene enhancer, kinase of
Nemo-/-

Leukocyte adhesion deficiency syndrome (LAD-III) and osteopetrosis
AR

Kindlin-3
Loss of function
Kindlin-3
Kind3-/_





AR

CalDAG-GEF1
Loss of function
Calcium and diacylglycerol-regulated guanine nucleotide exchange factor 1
CalDAG-GEF1-/-

Pycnodysostosis
AR
265800
CTSK
Loss of function
Cathepsin K
cathK-/-

Osteopoikilosis
AD
155950
LEMD3
Loss of function
LEM domain-containing 3


Melorheostosis with osteopoikilosis
AD
155950
LEMD3
Loss of function
LEM domain-containing 3


Dysosteosclerosis
AR
224300





Osteomesopyknosis
AD
166450





Osteopathia striata congenita with cranial stenosis
XL
300373
WTX
Loss of function
Wilms tumour gene on the X chromosome


Osteosclerosis, Stanescu type
AD
122900





Stark and Savarirayan Orphanet Journal of Rare Diseases 2009 4:5   doi:10.1186/1750-1172-4-5